A Patient & Family Story
College Student lives with Common Variable Immune Deficiency (CVID)
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Two-Year-Old Kamryn Living with Niemann-Pick Disease Type C (NPC)
Ugandan Family Visits Washington, D.C.
Leading Edge Treatment Gives Amber Hope
Research Helped Diagnose 6-Year-Old’s Rare Disease
T-cell Therapy Helping Acute Lymphoblastic Leukemia (ALL)
Makenna suffers from Blau Syndrome, rare inflammatory disorder
Sydney
Kayla & Cody
Niemann Pick Makes Julia Unique, Says Mom
