Treatment: Niemann-Pick Disease Type C

    Christina and mom Sue celebrate inside at The Inn

    A Patient & Family Story

    You Help Tina Face the Unimaginable With Courage

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    A Patient & Family Story

    Marlon Draws Strength From Family and Groundbreaking Trial

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    A family of 3 outside The Children's Inn

    A Patient & Family Story

    Two-Year-Old Kamryn Living with Niemann-Pick Disease Type C (NPC)

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